Development of LNA Gapmer Oligonucleotide-Based Therapy for ALS/FTD Caused by the C9orf72 Repeat Expansion.
Alzforum,
Sathyaprakash C, Manzano R, Varela MA, Hashimoto Y, Wood MJ, Talbot K, Aoki Y.
Sathyaprakash C, Manzano R, Varela MA, Hashimoto Y, Wood MJ, Talbot K, Aoki Y.
. Development of Antisense Oligonucleotide Gapmers for the Treatment of Huntington's Disease.